Objective:
To evaluate the impact of interventions in a focused home infusion/specialty pharmacy based inhibitor management program on patient outcomes including, adherence, retention, prescriber communication.
Methods…
Objective:
Kids A-LONG was a global, multi-center, open-label phase 3 study that evaluated the safety, efficacy, and pharmacokinetics (PK) of rFVIIIFc in previously treated patients aged <12 years with severe hemophilia A (…
Children with severe Hemophilia (CWH) suffer pain and inconvenience due to the required IV factor concentrates' injections and mostly exhibit poor quality of life. These children don't have any hope that their life will improve in the future. Most…
Objective:
Patient-centered medical home (PCMH), a team-based model of practice involving patients, families, providers and care team members, focuses on high quality, efficient, and patient-centered care. The purpose of this…
Introduction and Objective:
Prospective clinical trials have demonstrated the efficacy of prophylaxis in reducing bleeding episodes in hemophilia A and B patients and those with inhibitors. However, data, predominantly from…
Objective:
Using point-of-care musculoskeletal ultrasound (MSKUS), we previously demonstrated that patient and physician assessments were unreliable in determining bleeding during acute painful joint episodes. Here we delineated…
Objectives:
This prospective clinical trial was conducted to assess the safety, hemostatic efficacy and pharmacokinetic (PK) profile of a recently developed recombinant factor IX (BAX326*) in pediatric previously-treated patients…