Established Initiatives & Impact
The foundation's broad and diverse portfolio of brands and programming serve all those in the inheritable blood disorders community. Everyone – whether a patient, caregiver, loved one, or advocate – deserves accessible support and resources unique…
A multidisciplinary approach to the successful transition of a complex patient with severe hemophilia A with inhibitor to Emicizumab (Hemlibra®): A Case Study
Objective: Demonstrate the success of collaborative efforts between the specialized multidisciplinary Infusion Pharmacy Provider (IPP), the prescriber, patient and payer, in achieving improved outcomes. Methods:…
Review Offers Scientific Overview of AAV Vectors and Hemophilia Gene Therapy
In this review, the authors discuss some of the primary considerations relevant to investigational gene therapies that employ adeno-associated viral (AAV) vectors, with particular focus on immunogenicity and genotoxicity – the former denotes the…
New Descriptive Study Looks at Bleeding Disorder Camps
While it has been well established that bleeding disorders camps (BDCs) in the U.S. have played a key part in empowering affected children for decades, comprehensive knowledge of their capacity and functioning is historically lacking.In order to…
Rare Series: Current Treatments for Rare Bleeding Disorders
This session will discuss current treatment options for rare factor deficiencies and platelet dysfunctions. It will also provide practical tips about what information will foster an effective discussion with your hematology care provider about your…
Inhibitor Education Series: Ask the Experts
Do you have a burning question to ask our panel of experts? This session will offer participants an opportunity to interact, engage, and ask thought-provoking questions to a panel of interdisciplinary healthcare providers in real time.
Inhibitor Education Series: Baby Steps Navigating Past the Pandemic
After a challenging year driven by the COVID19 pandemic, we are looking forward to a new normal. But how does re-entering society impact mental health and what are specific implications for the bleeding disorder community? In this session, we will…
Rare Series: Baby Steps Navigating Past the Pandemic
After a challenging year driven by the COVID19 pandemic, we are looking forward to a new normal. But how does re-entering society impact mental health and what are specific implications for the bleeding disorder community? In this session, we will…
Pregunte a los expertos
¿Tiene una pregunta candente que hacerle a nuestro panel de expertos? Esta sesión ofrecerá a los participantes la oportunidad de interactuar, participar y hacer preguntas que inviten a la reflexión a un panel de proveedores de atención médica…
El Costo de la Reentrada
Después de un año difícil impulsado por la pandemia de COVID19, esperamos una nueva normalidad. Pero, ¿cómo afecta la reincorporación a la sociedad a la salud mental y cuáles son las implicaciones específicas para la comunidad de trastornos…