Dissecting the Roles of Non-muscle Myosin IIA in May-Hegglin Platelet Disorders
Per Dr. Pal, receiving the JGP Fellowship was a major milestone in her academic career and has given her the confidence to apply for future extramural funding.
Immunology of Liver-Derived Expression of Factor IX from AAV Vectors
Correction of Hemophilia with Lentiviral Vectors
Development and Characterization of Novel Genetically Engineered Factor VIII Molecules with Increased Activity and Stability
Gene Therapy for Hemophilia B by Direct Intramuscular Injections of Recombinant Adeno Associated Virus Serotype Vectors
Non-primate Lentiviral Vector-Based Gene Therapy for Hemophilia A
Nonviral Gene Delivery for Hemophilia
Gene Transfer of Factor VIII to the Liver in Vivo
Establishing the Factors Responsible for Hepatocyte Permissiveness to AAV Vectors
Retroviral Vector-Mediated Neonatal Gene Therapy for Hemophilia A