Novel Therapeutics for Hemophilia

Novel Therapeutics for Hemophilia

Year:
-
Grants:
Innovative Investigator Research Award
Hemophilia A (Factor VIII/F8)
Author(s):
Shannon L. Meeks

Dr. Meeks is an Associate Professor of Pediatrics in the Department of Pediatrics at the Emory University School of Medicine and the Aflac Cancer and Blood Disorders Center of Children’s Healthcare of Atlanta. She obtained a Bachelor of Science in Mathematics from Duke University where she was elected to Phi Beta Kappa. After earning her medical degree from the University of Mississippi, she completed her clinical training at the University of Virginia and Emory University. Dr. Meeks has a basic, translational, and clinical research interest in the development of inhibitors in hemophilia A. Her work has focused on the early immune response to factor VIII and the diversity of the B-cell response to factor VIII. She is a former NHF clinical fellow who currently has funding to pursue these projects from the Hemostasis and Thrombosis Research Society and the National Institutes of Health.

PiggyBac Mediated Gene Transfer for Coagulation Disorders

PiggyBac Mediated Gene Transfer for Coagulation Disorders

Year:
-
Grants:
Career Development Award
Gene Therapy
Author(s):
Janice M. Staber
Dr. Staber received her undergraduate e degree in biochemistry from the University of Iowa. She received her MD from the Carver College of Medicine at the University of lowa. She received strong mentorship under the guidance of Drs. Paul McCray and Steven Lentz during her post-doctoral research in gene therapy and hemophilia studies. She was subsequently appointed a faculty position at the University of Iowa Children's Hospital in 2010 and became Assistant Professor of Pediatrics in the Division of Hematology/Oncology in 2013.
HemoFOCUS Screener for Inattention, Hyperactivity and Impulsivity: A Quality Improvement Intervention for Children with Severe Hemophilia

HemoFOCUS Screener for Inattention, Hyperactivity and Impulsivity: A Quality Improvement Intervention for Children with Severe Hemophilia

Year: 2019
Grants:
Bleeding Disorders Conference
Psychosocial Issues
Author(s):
Amanda Pullen
Developing a Point-of-Care Testing for Hemophilia

Developing a Point-of-Care Testing for Hemophilia

Year:
-
Grants:
Innovative Investigator Research Award
Hemophilia A (Factor VIII/F8)
Author(s):
Jill M. Johnsen

Dr. Jill Johnsen is scientist and physician at the Washington Center for Bleeding Disorders in Seattle, WA.  She is an Associate Member at the Bloodworks Research Institute and also an Associate Professor of Medicine in the Division of Hematology at the University of Washington. Her research focuses on the study of hereditary and acquired modifiers of blood traits, with particular emphasis on the genetics and biology of variation in blood group and coagulation factors such as factor VIII, factor IX, and von Willebrand Factor.  Dr. Johnsen is honored by this award and grateful for this support that will further the development of a test to enable patients and providers to determine factor levels much more quickly without needing to send blood to a lab.

Clinical experience with BIVV001, the first investigational factor VIII (FVIII) therapy  to break through the von Willebrand factor (VWF) ceiling in hemophilia A

Clinical experience with BIVV001, the first investigational factor VIII (FVIII) therapy to break through the von Willebrand factor (VWF) ceiling in hemophilia A

Year: 2019
Grants:
Bleeding Disorders Conference
Clinical Research/Clinical Trials
Author(s):
Amy Shapiro, Doris V. Quon, Janice M Staber, Takashi Suzuki, Roshni Kulkarni, Margaret V. Ragni, Toshko Lissitchkov, Ekta Seth Chhabra, Stacey Poloskey, Barbara A. Konkle, Kara Rice, Suresh Katragadda, Joachim Fruebis