Stay informed with the latest updates for the inheritable blood disorders community.

          Medical
          Sickle Cell
          FDA Approves Pair of Cell-Based Gene Therapies for Sickle Cell Disease
          Interview with 2023 NYLI Cohort Member Paxton Mills
          NBDF & Community
          Ampoule bottles on an assembly line
          Novo Seven Unavailable in 8 mg Vials Due to Supply…
          Advocacy & Legislative
          Government Relations Update - November 2023
          Industry
          FDA Grants Expanded Approval to Wilate® for Prophylaxis in All Types of…
          Press Releases
          NBDF Announces 2023 Kevin Child Scholarship Winner
          Industry
          First Patient Dosed with Hemophilia Gene Therapy Candidate ASC618
          NBDF & Community
          Transgender flag
          The Importance of Transgender Health: Interview with Alexis Dinno
          Industry
          Sernova Receives Dual FDA Designations for Investigational Hemophilia…
          NBDF & Community
          Transgender flag
          Transgender Health and the Bleeding Disorders Community: An…
          Medical
          FDA Approves Recombinant Therapy for Congenital Thrombotic…
          Medical
          Study Suggests Racial and Ethnic Disparities in Hemophilia and ITI
          Medical
          Photo of a podium and microphone
          New Hemophilia Gene Therapy Video Presentations Available
          Medical
          Hepatocellular Cancer Screening and Gene Therapy…
          Advocacy & Legislative
          Capital Building
          NBDF Government Relations Update - October 2023