Stay informed with the latest updates for the inheritable blood disorders community.

Industry
Gene Therapy Helix
Integration of Spark into Roche Group Set, Hemophilia Gene…
Industry
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First Patient Dosed with Investigational Sub-Q Therapy for von…
Industry
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Pfizer Discontinues Beqvez Hemophilia B Gene Therapy
Industry
Red blood cells bone marrow
Investigational Sub-Q Von Willebrand Disease Therapy Put on Fast Track
Industry
DNA structure
Trial Updates for Investigational Hemophilia A Gene Therapy Shared at ASH…
Industry
A person pointing at their arm with purple spots
Sanofi Announces Positive Data for Its Investigational ITP Therapy
Industry
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Star Therapeutics Presents Data on Investigational VWD Therapy
Industry
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BioMarin to Narrow Its Commercial Focus for Hemophilia A Gene Therapy
Industry
Gene Therapy a pill with DNA
Pfizer Announces New Data from Hemophilia A Gene Therapy Study
Industry
FDA Approval Includes Full ALTUVIIIO™ Pediatric Trial Results
Industry
Gene Therapy
Hemophilia B Gene Therapy Trial Data Published
Industry
Persons hand with a rash
Takeda Announces Interim Trial Results for Investigational ITP Therapy
Industry
uniQure Announces Findings from HCC Case Investigation in HOPE-B Trial for Gene Therapy
Takeda's Voluntary Withdrawal: Alert on Misprinted Labels for VONVENDI®
Industry
FDA Accepts Biologics License Application for Marstacimab
Industry
CSL Presents Three Year Treatment Data for Hemophilia B Gene Therapy