Stay informed with the latest updates for the inheritable blood disorders community.

Industry
Takeda Announces Trial Results on Investigational Therapy for Ultra Rare Blood Disorder
Takeda Announces Trial Results on Investigational Therapy for…
Industry
Image of a blue gene helix with a red section in the center
Pfizer Announces Trial Updates for Investigational Hemophilia Gene Therapy…
Industry
Clinical Trial Lab Research
Spark Announces SPK-8011 Updates at ASH
Industry
BioMarin Shares Community Update for Valoctocogene Roxaparvovec
BioMarin Shares Community Update for Valoctocogene Roxaparvovec
Industry
Clinical Trial Gene Therapy Double Helix
Recruitment Reopened for Phase 3 AFFINE Gene Therapy Trial
Industry
Red Blood Cells
FDA Grants Priority Review for Sanofi’s BIVV001
Industry
Doctor asking questions to patient about care
Rare Factor X Deficiency Survey Shows Disparity in Care
Industry
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BioMarin Receives Conditional Approval in Europe for Gene Therapy
Industry
BioMarin Presents Abstract on Vector DNA Transmission Risk at ISTH
BioMarin Presents Abstract on Vector DNA Transmission Risk at ISTH
Industry
New Prophylaxis Approval for REBINYN®
New Prophylaxis Approval for REBINYN®
Industry
Sanofi Provides Fitusiran Trial Updates at ISTH
Sanofi Provides Fitusiran Trial Updates at ISTH
Industry
Prophylactic Therapy for Glanzmann Thrombasthenia Moves Towards Clinical Trials
Prophylactic Therapy for Glanzmann Thrombasthenia Moves Towards…
Industry
Scientist using Microscope in a clinical trial
Sanofi and Sobi® Report Progress with BIVV001 at International Congress
Industry
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Bayer Announces Discontinuation of Kogenate® FS
Industry
Blood Cells Image
FDA Grants Breakthrough Status to BIVV001