NBDF showcases a wide array of findings from the latest in bleeding disorders research at our annual Bleeding Disorders Conference.
Five-year safety and efficacy of N8-GP (ESPEROCT®) in previously treated children with hemophilia A in the completed pathfinder 5 trial
AWARDED/PRESENTED: 2019
GRANT/PROGRAM:
Bleeding Disorders Conference
Clinical Research/Clinical Trials
Quality of life and health in patients with Haemophilia in Mexico
AWARDED/PRESENTED: 2019
GRANT/PROGRAM:
Bleeding Disorders Conference
Quality of Life/Outcomes Research
Four-year safety and efficacy of N8-GP (ESPEROCT®) in previously treated adolescents/adults with hemophilia A in the completed pathfinder 2 trial
AWARDED/PRESENTED: 2019
GRANT/PROGRAM:
Bleeding Disorders Conference
Clinical Research/Clinical Trials
Patients Report High Satisfaction with US Hemophilia Treatment Centers: National Trends 2014 and 2017
AWARDED/PRESENTED: 2019
GRANT/PROGRAM:
Bleeding Disorders Conference
Quality of Life/Outcomes Research
Navigating the Emergency Department: A Collaboration Among Hemophilia Treatment Center Staff, Emergency Department Staff & Bleeding Disorder Chapter Staff
AWARDED/PRESENTED: 2019
GRANT/PROGRAM:
Bleeding Disorders Conference
Collaboration/Team Models
Patient Perspectives on the Impact of Severe or Moderate Hemophilia on Physical Activity: HemACTIVE Survey Findings from the US and Canada
AWARDED/PRESENTED: 2019
GRANT/PROGRAM:
Bleeding Disorders Conference
Quality of Life/Outcomes Research
rFVIIIFc for first-time immune tolerance induction therapy: interim results from the global, prospective verITI-8 study
AWARDED/PRESENTED: 2019
GRANT/PROGRAM:
Bleeding Disorders Conference
Inhibitors
World Federation of Hemophilia Annual Global Survey 2017 – 19 years of reporting
AWARDED/PRESENTED: 2019
GRANT/PROGRAM:
Bleeding Disorders Conference
Quality of Life/Outcomes Research
Validation of a FVIII Chromogenic Nijmegen Bethesda Assay for the Detection of Inhibitors in the Presence of Emicizumab (ACE-910)
AWARDED/PRESENTED: 2019
GRANT/PROGRAM:
Bleeding Disorders Conference
Inhibitors
The Patient Reported Outcomes Burdens and Experiences (PROBE) Study Questionnaire Development and Validation
AWARDED/PRESENTED: 2019
GRANT/PROGRAM:
Bleeding Disorders Conference
Quality of Life/Outcomes Research
Achievement of therapeutic levels of factor VIII activity following gene transfer with valoctocogene roxaparvovec (BMN 270): Long-term efficacy and safety results in patients with severe hemophilia A
AWARDED/PRESENTED: 2018
GRANT/PROGRAM:
Bleeding Disorders Conference
Clinical Research/Clinical Trials
Annual Bleed Rates Compared Before and After Changing to Extended Half Life Products in Home Infusion Patients with severe hemophilia
AWARDED/PRESENTED: 2018
GRANT/PROGRAM:
Bleeding Disorders Conference
Clinical Research/Clinical Trials
Long-term Benefit of BAY 81-8973 Prophylaxis in Children With Severe Hemophilia A: Interim Analysis of the LEOPOLD Kids Extension Study
AWARDED/PRESENTED: 2018
GRANT/PROGRAM:
Bleeding Disorders Conference
Clinical Research/Clinical Trials
Impact of hemophilia on employment - Insights from the PROBE Study
AWARDED/PRESENTED: 2018
GRANT/PROGRAM:
Bleeding Disorders Conference
Quality of Life/Outcomes Research
Empowering the Future of Hemophilia Through Swimming (Poster Abstract)
AWARDED/PRESENTED: 2018
GRANT/PROGRAM:
Bleeding Disorders Conference
Psychosocial Issues
Effects of Factor VIII Prophylaxis on Vascular Remodeling and Synovial Gene Expression Changes Associated with Hemarthrosis in FVIII-Deficient Mice
AWARDED/PRESENTED: 2018
GRANT/PROGRAM:
Bleeding Disorders Conference
Biomedical/Coagulation Research
Efficacy of on-demand treatment of bleeding episodes in hemophilia B patients with extended half-life N9-GP in pivotal trials: an in-depth analysis of treatment
AWARDED/PRESENTED: 2018
GRANT/PROGRAM:
Bleeding Disorders Conference
Clinical Research/Clinical Trials
Retrospective review of unplanned hospitalizations and perceived pain in children and adults with a diagnosis of factor ten deficiency receiving home infusions of commercially available factor ten
AWARDED/PRESENTED: 2018
GRANT/PROGRAM:
Bleeding Disorders Conference
New Products
Persons With Hemophilia Reinforce Their Desire to be More Active: US Findings From an International Patient Survey
AWARDED/PRESENTED: 2018
GRANT/PROGRAM:
Bleeding Disorders Conference
Quality of Life/Outcomes Research
The Relationship of Hope and Self-Compassion with Quality of Life among Individuals with Bleeding Disorders
AWARDED/PRESENTED: 2018
GRANT/PROGRAM:
Bleeding Disorders Conference
Psychosocial Issues