Awarded/Presented
Tags
CVR
Researchers
Jacqueline Limjoco, Agustin Calatroni, Paula Aristizabal, Courtney D Thornburg
The aim of this study was to evaluate preferences and variables which influence decision-making related to gene therapy and other novel haemophilia therapies. Haemophilia Treatment Centers and patient advocacy groups must be able to educate persons with haemophilia about aspects of novel therapies which are important to the individual, especially short- and long-term safety and efficacy.